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Vision loss in juvenile neuronal ceroid lipofuscinosis (CLN3 disease)

Juvenile neuronal ceroid lipofuscinosis (JNCL; also known as CLN3 disease) is a devastating neurodegenerative lysosomal storage disorder and the most common form of Batten disease. Progressive visual and neurological symptoms lead to mortality in patients by the third decade. Although ceroid-lipofus...

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Detalhes bibliográficos
Publicado no:Ann N Y Acad Sci
Main Authors: Ouseph, Madhu M., Kleinman, Mark E., Wang, Qing Jun
Formato: Artigo
Idioma:Inglês
Publicado em: 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5025599/
https://ncbi.nlm.nih.gov/pubmed/26748992
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/nyas.12990
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