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Treatment with l-citrulline and metformin in Duchenne muscular dystrophy: study protocol for a single-centre, randomised, placebo-controlled trial

BACKGROUND: Duchenne muscular dystrophy (DMD) is an X-linked recessive disease that affects 1 in 3500–6000 male births. Despite broad research aiming to improve muscle function as well as heart and brain function, sufficient therapeutic efficacy has not yet been achieved and current therapeutic mana...

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Dettagli Bibliografici
Pubblicato in:Trials
Autori principali: Hafner, Patricia, Bonati, Ulrike, Rubino, Daniela, Gocheva, Vanya, Zumbrunn, Thomas, Gueven, Nuri, Fischer, Dirk
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4973063/
https://ncbi.nlm.nih.gov/pubmed/27488051
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13063-016-1503-1
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