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Efficacy of lumacaftor-ivacaftor for the treatment of cystic fibrosis patients homozygous for the F508del-CFTR mutation

Cystic fibrosis (CF) results from mutations in the CF transmembrane conductance regulator (CFTR) gene, which codes for the CFTR channel protein. The most common mutation in CF is F508del, which produces a misfolded protein with diminished channel activity. The development of small-molecule CFTR-modu...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Expert Rev Precis Med Drug Dev
Egile Nagusiak: Cholon, Deborah M., Esther, Charles R., Gentzsch, Martina
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2016
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC4963025/
https://ncbi.nlm.nih.gov/pubmed/27482545
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1080/23808993.2016.1175299
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