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Efficacy of lumacaftor-ivacaftor for the treatment of cystic fibrosis patients homozygous for the F508del-CFTR mutation

Cystic fibrosis (CF) results from mutations in the CF transmembrane conductance regulator (CFTR) gene, which codes for the CFTR channel protein. The most common mutation in CF is F508del, which produces a misfolded protein with diminished channel activity. The development of small-molecule CFTR-modu...

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Publicado en:Expert Rev Precis Med Drug Dev
Autores principales: Cholon, Deborah M., Esther, Charles R., Gentzsch, Martina
Formato: Artigo
Lenguaje:Inglês
Publicado: 2016
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC4963025/
https://ncbi.nlm.nih.gov/pubmed/27482545
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1080/23808993.2016.1175299
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