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Zinc-finger nuclease-mediated gene correction using single AAV vector transduction and enhancement by Food and Drug Administration-approved drugs

An emerging strategy for the treatment of monogenic diseases uses genetic engineering to precisely correct the mutation(s) at the genome level. Recent advancements in this technology have demonstrated therapeutic levels of gene correction using a zinc-finger nuclease (ZFN)-induced DNA double-strand...

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Dettagli Bibliografici
Pubblicato in:Gene Ther
Autori principali: Ellis, BL, Hirsch, ML, Porter, SN, Samulski, RJ, Porteus, MH
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2012
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4957644/
https://ncbi.nlm.nih.gov/pubmed/22257934
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/gt.2011.211
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