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Rescue of the Functional Alterations of Motor Cortical Circuits in Arginase Deficiency by Neonatal Gene Therapy

Arginase 1 deficiency is a urea cycle disorder associated with hyperargininemia, spastic diplegia, loss of ambulation, intellectual disability, and seizures. To gain insight on how loss of arginase expression affects the excitability and synaptic connectivity of the cortical neurons in the developin...

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Pubblicato in:J Neurosci
Autori principali: Cantero, Gloria, Liu, Xiao-Bo, Mervis, Ronald F., Lazaro, Maria T., Cederbaum, Stephen D., Golshani, Peyman, Lipshutz, Gerald S.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Society for Neuroscience 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4916246/
https://ncbi.nlm.nih.gov/pubmed/27335400
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1523/JNEUROSCI.0897-16.2016
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