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A Novel Functional Missense Mutation p.T219A in Type 1 Gaucher's Disease

BACKGROUND: Gaucher's disease (GD) is an autosomal recessive disorder caused by a deficiency of acid β-glucosidase (glucocerebrosidase [GBA]) that results in the accumulation of glucocerebroside within macrophages. Many mutations have been reported to be associated with this disorder. This stud...

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Publicat a:Chin Med J (Engl)
Autors principals: Liu, Lin-Yu, Liu, Fei, Du, Si-Chen, Jiang, Sha-Yi, Wang, Hui-Jun, Zhang, Jin, Wang, Wei, Ma, Duan
Format: Artigo
Idioma:Inglês
Publicat: Medknow Publications & Media Pvt Ltd 2016
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4852675/
https://ncbi.nlm.nih.gov/pubmed/27098793
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4103/0366-6999.180523
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