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Efficacy and Safety of Sirolimus in the Treatment of Complicated Vascular Anomalies

BACKGROUND AND OBJECTIVES: Complicated vascular anomalies have limited therapeutic options and cause significant morbidity and mortality. This Phase II trial enrolled patients with complicated vascular anomalies to determine the efficacy and safety of treatment with sirolimus for 12 courses; each co...

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Detalhes bibliográficos
Publicado no:Pediatrics
Main Authors: Adams, Denise M., Trenor, Cameron C., Hammill, Adrienne M., Vinks, Alexander A., Patel, Manish N., Chaudry, Gulraiz, Wentzel, Mary Sue, Mobberley-Schuman, Paula S., Campbell, Lisa M., Brookbank, Christine, Gupta, Anita, Chute, Carol, Eile, Jennifer, McKenna, Jesse, Merrow, Arnold C., Fei, Lin, Hornung, Lindsey, Seid, Michael, Dasgupta, A. Roshni, Dickie, Belinda H., Elluru, Ravindhra G., Lucky, Anne W., Weiss, Brian, Azizkhan, Richard G.
Formato: Artigo
Idioma:Inglês
Publicado em: American Academy of Pediatrics 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4732362/
https://ncbi.nlm.nih.gov/pubmed/26783326
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1542/peds.2015-3257
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