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Efficacy of Systemic Sirolimus in the Treatment of Generalized Lymphatic Anomaly and Gorham-Stout Disease

BACKGROUND: Generalized lymphatic anomaly (GLA) and Gorham-Stout disease (GSD) are rare complicated lymphatic malformations that occur in multiple body sites and are associated with significant morbidity and mortality. Treatment options have been limited and conventional medical therapies have been...

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Detalhes bibliográficos
Publicado no:Pediatr Blood Cancer
Main Authors: Ricci, Kiersten W., Hammill, Adrienne M., Mobberley-Schuman, Paula, Nelson, Stephen C., Blatt, Julie, Glade Bender, Julia L., McCuaig, Catherine C., Synakiewicz, Anna, Frieden, Ilona J., Adams, Denise M.
Formato: Artigo
Idioma:Inglês
Publicado em: 2019
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6428616/
https://ncbi.nlm.nih.gov/pubmed/30672136
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/pbc.27614
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