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Efficacy of Systemic Sirolimus in the Treatment of Generalized Lymphatic Anomaly and Gorham-Stout Disease

BACKGROUND: Generalized lymphatic anomaly (GLA) and Gorham-Stout disease (GSD) are rare complicated lymphatic malformations that occur in multiple body sites and are associated with significant morbidity and mortality. Treatment options have been limited and conventional medical therapies have been...

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Publicado en:Pediatr Blood Cancer
Autores principales: Ricci, Kiersten W., Hammill, Adrienne M., Mobberley-Schuman, Paula, Nelson, Stephen C., Blatt, Julie, Glade Bender, Julia L., McCuaig, Catherine C., Synakiewicz, Anna, Frieden, Ilona J., Adams, Denise M.
Formato: Artigo
Lenguaje:Inglês
Publicado: 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6428616/
https://ncbi.nlm.nih.gov/pubmed/30672136
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/pbc.27614
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