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Efficacy of Systemic Sirolimus in the Treatment of Generalized Lymphatic Anomaly and Gorham-Stout Disease

BACKGROUND: Generalized lymphatic anomaly (GLA) and Gorham-Stout disease (GSD) are rare complicated lymphatic malformations that occur in multiple body sites and are associated with significant morbidity and mortality. Treatment options have been limited and conventional medical therapies have been...

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Dettagli Bibliografici
Pubblicato in:Pediatr Blood Cancer
Autori principali: Ricci, Kiersten W., Hammill, Adrienne M., Mobberley-Schuman, Paula, Nelson, Stephen C., Blatt, Julie, Glade Bender, Julia L., McCuaig, Catherine C., Synakiewicz, Anna, Frieden, Ilona J., Adams, Denise M.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2019
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6428616/
https://ncbi.nlm.nih.gov/pubmed/30672136
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/pbc.27614
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