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Sirolimus is effective in relapsed/refractory autoimmune cytopenias: results of a prospective multi-institutional trial

Patients with autoimmune multilineage cytopenias are often refractory to standard therapies requiring chronic immunosuppression with medications with limited efficacy and high toxicity. We present data on 30 patients treated on a multicenter prospective clinical trial using sirolimus as monotherapy....

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Publicat a:Blood
Autors principals: Bride, Karen L., Vincent, Tiffaney, Smith-Whitley, Kim, Lambert, Michele P., Bleesing, Jack J., Seif, Alix E., Manno, Catherine S., Casper, James, Grupp, Stephan A., Teachey, David T.
Format: Artigo
Idioma:Inglês
Publicat: American Society of Hematology 2016
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4705607/
https://ncbi.nlm.nih.gov/pubmed/26504182
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2015-07-657981
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