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Production of gene-corrected adult beta globin protein in human erythrocytes differentiated from patient iPSCs after genome editing of the sickle point mutation

Human induced pluripotent stem cells (iPSCs) and genome editing provide a precise way to generate gene-corrected cells for disease modeling and cell therapies. Human iPSCs generated from sickle cell disease (SCD) patients have a homozygous missense point mutation in the HBB gene encoding adult β-glo...

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Bibliografiske detaljer
Udgivet i:Stem Cells
Main Authors: Huang, Xiaosong, Wang, Ying, Yan, Wei, Smith, Cory, Ye, Zhaohui, Wang, Jing, Gao, Yongxing, Mendelsohn, Laurel, Cheng, Linzhao
Format: Artigo
Sprog:Inglês
Udgivet: 2015
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC4628786/
https://ncbi.nlm.nih.gov/pubmed/25702619
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/stem.1969
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