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Effect of Readthrough Treatment in Fibroblasts of Patients Affected by Lysosomal Diseases Caused by Premature Termination Codons

Aminoglycoside antibiotics, such as gentamicin, may induce premature termination codon (PTC) readthrough and elude the nonsense-mediated mRNA decay mechanism. Because PTCs are frequently involved in lysosomal diseases, readthrough compounds may be useful as potential therapeutic agents. The aim of o...

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Publicat a:Neurotherapeutics
Autors principals: Matalonga, Leslie, Arias, Ángela, Tort, Frederic, Ferrer-Cortés, Xènia, Garcia-Villoria, Judit, Coll, Maria Josep, Gort, Laura, Ribes, Antonia
Format: Artigo
Idioma:Inglês
Publicat: Springer US 2015
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4604176/
https://ncbi.nlm.nih.gov/pubmed/26169295
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s13311-015-0368-4
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