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From Infancy to Adolescence: Fifteen Years of Continuous Treatment With Hydroxyurea in Sickle Cell Anemia

Despite documented laboratory and clinical benefits of hydroxyurea for children with sickle cell anemia (SCA), the drug's long-term safety and efficacy remains poorly defined. The HUSOFT trial and extension study examined feasibility, toxicity, and hematological efficacy of hydroxyurea in infan...

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Библиографические подробности
Опубликовано в: :Medicine (Baltimore)
Главные авторы: Hankins, Jane S., Aygun, Banu, Nottage, Kerri, Thornburg, Courtney, Smeltzer, Matthew P., Ware, Russell E., Wang, Winfred C.
Формат: Artigo
Язык:Inglês
Опубликовано: Wolters Kluwer Health 2014
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC4603125/
https://ncbi.nlm.nih.gov/pubmed/25526439
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MD.0000000000000215
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