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Increasing the minicircle DNA purity using an enhanced triplex DNA technology to eliminate DNA contaminants

DNA vectors for human gene therapy have to meet the efficacy and safety requirements. Minicircles (MCs), a class of optimized DNA vectors free of plasmid backbone (PB) DNAs, have emerged as promising candidates because of their superior transgene expression profiles. However, the existence of impure...

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Dettagli Bibliografici
Pubblicato in:Mol Ther Methods Clin Dev
Autori principali: Hou, Xiaohu H, Guo, Xiaoyan Y, Chen, Yusheng, He, Cheng-Yi, Chen, Zhi-Ying
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group 2015
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4449018/
https://ncbi.nlm.nih.gov/pubmed/26052527
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mtm.2014.62
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