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A novel missense mutation in the GNE gene in an Iranian patient with hereditary inclusion body myopathy

Hereditary inclusion body myopathy (hIBM) is an adult-onset hereditary myopathy, usually with distal onset and quadriceps sparing. This myopathy is autosomal recessive and associated to UPD-N-acetylglucosamine-2-epimerase/N-acetylmannosamine kinase (GNE) gene mutations. In this study, we report a no...

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Publicat a:J Res Med Sci
Autors principals: Behnam, Mahdiyeh, Jin-Hong, Shin, Kim, Dae-Seong, Basiri, Keivan, Nilipour, Yalda, Sedghi, Maryam
Format: Artigo
Idioma:Inglês
Publicat: Medknow Publications & Media Pvt Ltd 2014
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4235102/
https://ncbi.nlm.nih.gov/pubmed/25422667
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