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Preclinical Assessment of wt GNE Gene Plasmid for Management of Hereditary Inclusion Body Myopathy 2 (HIBM2)

Hereditary Inclusion Body Myopathy (HIBM2) is a chronic progressive skeletal muscle wasting disorder which generally leads to complete disability before the age of 50 years. There is currently no effective therapeutic treatment for HIBM2. Development of this disease is related to expression in famil...

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Главные авторы: Jay, Chris, Nemunaitis, Gregory, Nemunaitis, John, Senzer, Neil, Hinderlich, Stephan, Darvish, Daniel, Ogden, Julie, Eager, John, Tong, Alex, Maples, Phillip B
Формат: Artigo
Язык:Inglês
Опубликовано: Libertas Academica 2008
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC2733101/
https://ncbi.nlm.nih.gov/pubmed/19787087
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