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Organizing national responses for rare blood disorders: the Italian experience with sickle cell disease in childhood

BACKGROUND: Sickle cell disease (SCD) is the most frequent hemoglobinopathy worldwide but remains a rare blood disorder in most western countries. Recommendations for standard of care have been produced in the United States, the United Kingdom and France, where this disease is relatively frequent be...

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Detalhes bibliográficos
Publicado no:Orphanet J Rare Dis
Main Authors: Colombatti, Raffaella, Perrotta, Silverio, Samperi, Piera, Casale, Maddalena, Masera, Nicoletta, Palazzi, Giovanni, Sainati, Laura, Russo, Giovanna
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2013
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4231397/
https://ncbi.nlm.nih.gov/pubmed/24139596
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1750-1172-8-169
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