Carregant...

Targeted Exon Skipping to Correct Exon Duplications in the Dystrophin Gene

Duchenne muscular dystrophy is a severe muscle-wasting disease caused by mutations in the dystrophin gene that ablate functional protein expression. Although exonic deletions are the most common Duchenne muscular dystrophy lesion, duplications account for 10–15% of reported disease-causing mutations...

Descripció completa

Guardat en:
Dades bibliogràfiques
Autors principals: Greer, Kane L, Lochmüller, Hanns, Flanigan, Kevin, Fletcher, Susan, Wilton, Steve D
Format: Artigo
Idioma:Inglês
Publicat: Nature Publishing Group 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3982197/
https://ncbi.nlm.nih.gov/pubmed/24643206
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mtna.2014.8
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!