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Whole Exome Sequencing of a Dominant Retinitis Pigmentosa Family Identifies a Novel Deletion in PRPF31

PURPOSE. Mutations at some retinitis pigmentosa (RP) loci are associated with variable penetrance and expressivity, exacerbating diagnostic challenges. The purpose of this study was to dissect the genetic underpinnings of nonsyndromic RP with variable age of onset in a large Mexican family. METHODS....

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Detalhes bibliográficos
Main Authors: Villanueva, Adda, Willer, Jason R., Bryois, Julien, Dermitzakis, Emmanouil T., Katsanis, Nicholas, Davis, Erica E.
Formato: Artigo
Idioma:Inglês
Publicado em: The Association for Research in Vision and Ophthalmology 2014
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3979517/
https://ncbi.nlm.nih.gov/pubmed/24595387
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1167/iovs.13-13827
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