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Course of Ocular Function in PRPF31 Retinitis Pigmentosa

Mutations in pre-mRNA splicing factors are the second most common cause of autosomal dominant retinitis pigmentosa, and a major cause of vision loss [1–3]. The development of gene augmentation therapy for disease caused by mutations in PRPF31 necessitates defining pre-treatment characteristics and d...

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Dettagli Bibliografici
Pubblicato in:Semin Ophthalmol
Autori principali: Hafler, Brian P., Comander, Jason, DiFranco, Carol Weigel, Place, Emily M., Pierce, Eric A.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6377939/
https://ncbi.nlm.nih.gov/pubmed/26959129
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3109/08820538.2015.1114856
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