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Correction of Nonsense BMPR2 and SMAD9 Mutations by Ataluren in Pulmonary Arterial Hypertension

Heritable pulmonary arterial hypertension (HPAH) is a serious lung vascular disease caused by heterozygous mutations in the bone morphogenetic protein (BMP) pathway genes, BMPR2 and SMAD9. One noncanonical function of BMP signaling regulates biogenesis of a subset of microRNAs. We have previously sh...

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Autori principali: Drake, Kylie M., Dunmore, Benjamin J., McNelly, Lauren N., Morrell, Nicholas W., Aldred, Micheala A.
Natura: Artigo
Lingua:Inglês
Pubblicazione: American Thoracic Society 2013
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3824059/
https://ncbi.nlm.nih.gov/pubmed/23590310
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1165/rcmb.2013-0100OC
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