ロード中...

Intrapleural Administration of AAV9 Improves Neural and Cardiorespiratory Function in Pompe Disease

Pompe disease is a neuromuscular disease resulting from deficiency in acid α-glucosidase (GAA), results in cardiac, skeletal muscle, and central nervous system (CNS) pathology. Enzyme replacement therapy (ERT) has been shown to partially correct cardiac and skeletal muscle dysfunction. However, ERT...

詳細記述

保存先:
書誌詳細
主要な著者: Falk, Darin J, Mah, Cathryn S, Soustek, Meghan S, Lee, Kun-Ze, ElMallah, Mai K, Cloutier, Denise A, Fuller, David D, Byrne, Barry J
フォーマット: Artigo
言語:Inglês
出版事項: Nature Publishing Group 2013
主題:
オンライン・アクセス:https://ncbi.nlm.nih.gov/pmc/articles/PMC3776643/
https://ncbi.nlm.nih.gov/pubmed/23732990
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2013.96
タグ: タグ追加
タグなし, このレコードへの初めてのタグを付けませんか!