Загрузка...

Clearance of lysosomal glycogen accumulation by Transcription factor EB (TFEB) in muscle cells from lysosomal alpha-glucosidase deficient mice

A recently proposed therapeutic approach for lysosomal storage disorders (LSDs) relies upon the ability of transcription factor EB (TFEB) to stimulate autophagy and induce lysosomal exocytosis leading to cellular clearance. This approach is particularly attractive in Glycogen Storage Disease type II...

Полное описание

Сохранить в:
Библиографические подробности
Главные авторы: Li, Hoi Ming, Feeney, Erin, Li, Lishu, Zare, Hossein, Puertollano, Rosa, Raben, Nina
Формат: Artigo
Язык:Inglês
Опубликовано: 2013
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC3687018/
https://ncbi.nlm.nih.gov/pubmed/23416076
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.bbrc.2013.02.026
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!