Pompe disease- experience from South India

Eitemau Tebyg

• Long term outcome and clinical experience on immune tolerance induction therapies in infantile Pompe disease
  gan: Austin, Stephanie, et al.
  Cyhoeddwyd: (2013)
• Clinical laboratory experience of blood CRIM testing in infantile Pompe disease
  gan: Bali, Deeksha S., et al.
  Cyhoeddwyd: (2015)
• Spectrum of Pompe disease in childhood – The Toronto experience
  gan: Raiman, J, et al.
  Cyhoeddwyd: (2013)
• The Pompe Registry: tracking Pompe disease symptoms in a broad patient population
  gan: Byrne, B, et al.
  Cyhoeddwyd: (2008)
• Liver depot gene therapy for Pompe disease
  gan: Kishnani, Priya S., et al.
  Cyhoeddwyd: (2019)