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Pupillometric analysis for assessment of gene therapy in Leber Congenital Amaurosis patients

BACKGROUND: Objective techniques to assess the amelioration of vision in patients with impaired visual function are needed to standardize efficacy assessment in gene therapy trials for ocular diseases. Pupillometry has been investigated in several diseases in order to provide objective information a...

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Autori principali: Melillo, Paolo, Pecchia, Leandro, Testa, Francesco, Rossi, Settimio, Bennett, Jean, Simonelli, Francesca
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2012
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3526436/
https://ncbi.nlm.nih.gov/pubmed/22812667
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1475-925X-11-40
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