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Pupillometric analysis for assessment of gene therapy in Leber Congenital Amaurosis patients

BACKGROUND: Objective techniques to assess the amelioration of vision in patients with impaired visual function are needed to standardize efficacy assessment in gene therapy trials for ocular diseases. Pupillometry has been investigated in several diseases in order to provide objective information a...

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Autores principales: Melillo, Paolo, Pecchia, Leandro, Testa, Francesco, Rossi, Settimio, Bennett, Jean, Simonelli, Francesca
Formato: Artigo
Lenguaje:Inglês
Publicado: BioMed Central 2012
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC3526436/
https://ncbi.nlm.nih.gov/pubmed/22812667
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1475-925X-11-40
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