Laddar...
Safety and Efficacy of Gene Transfer for Leber’s Congenital Amaurosis
Leber’s congenital amaurosis (LCA) is a group of inherited blinding diseases with onset during childhood. One form of the disease, LCA2, is caused by mutations in the retinal pigment epithelium–specific 65-kDa protein gene (RPE65). We investigated the safety of subretinal delivery of a recombinant a...
Sparad:
| Huvudupphovsmän: | , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , |
|---|---|
| Materialtyp: | Artigo |
| Språk: | Inglês |
| Publicerad: |
2008
|
| Ämnen: | |
| Länkar: | https://ncbi.nlm.nih.gov/pmc/articles/PMC2829748/ https://ncbi.nlm.nih.gov/pubmed/18441370 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1056/NEJMoa0802315 |
| Taggar: |
Lägg till en tagg
Inga taggar, Lägg till första taggen!
|