The human visual cortex responds to gene therapy–mediated recovery of retinal function

Por Ashtari, Manzar, Cyckowski, Laura L., Monroe, Justin F., Marshall, Kathleen A., Chung, Daniel C., Auricchio, Alberto, Simonelli, Francesca, Leroy, Bart P., Maguire, Albert M., Shindler, Kenneth S., Bennett, Jean
Publicado em 2011

The human visual cortex responds to gene therapy–mediated recovery of retinal function

Por Ashtari, Manzar, Cyckowski, Laura L., Monroe, Justin F., Marshall, Kathleen A., Chung, Daniel C., Auricchio, Alberto, Simonelli, Francesca, Leroy, Bart P., Maguire, Albert M., Shindler, Kenneth S., Bennett, Jean
Publicado em 2011

Plasticity of the human visual system after retinal gene therapy in patients with Leber’s congenital amaurosis

Por Ashtari, Manzar, Zhang, Hui, Cook, Philip A., Cyckowski, Laura L., Shindler, Kenneth S., Marshall, Kathleen A., Aravand, Puya, Vossough, Arastoo, Gee, James C., Maguire, Albert M., Baker, Chris I., Bennett, Jean
Publicado no Sci Transl Med (2015)

AAV2 Gene Therapy Readministration in Three Adults with Congenital Blindness

Por Bennett, Jean, Ashtari, Manzar, Wellman, Jennifer, Marshall, Kathleen A., Cyckowski, Laura L., Chung, Daniel C., McCague, Sarah, Pierce, Eric A., Chen, Yifeng, Bennicelli, Jeannette L., Zhu, Xiaosong, Ying, Gui-shuang, Sun, Junwei, Wright, J. Fraser, Auricchio, Alberto, Simonelli, Francesca, Shindler, Kenneth S., Mingozzi, Federico, High, Katherine A., Maguire, Albert M.
Publicado em 2012

Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutatons: a follow-on phase 1 tr...

Por Bennett, Jean, Wellman, Jennifer, Marshall, Kathleen A, McCague, Sarah, Ashtari, Manzar, DiStefano-Pappas, Julie, Elci, Okan U, Chung, Daniel C, Sun, Junwei, Wright, J Fraser, Cross, Dominique R, Aravand, Puya, Cyckowski, Laura L, Bennicelli, Jeannette L, Mingozzi, Federico, Auricchio, Alberto, Pierce, Eric A, Ruggiero, Jason, Leroy, Bart P, Simonelli, Francesca, High, Katherine A, Maguire, Albert M
Publicado no Lancet (2016)

Safety and Efficacy of Gene Transfer for Leber’s Congenital Amaurosis

Por Maguire, Albert M., Simonelli, Francesca, Pierce, Eric A., Pugh, Edward N., Mingozzi, Federico, Bennicelli, Jeannette, Banfi, Sandro, Marshall, Kathleen A., Testa, Francesco, Surace, Enrico M., Rossi, Settimio, Lyubarsky, Arkady, Arruda, Valder R., Konkle, Barbara, Stone, Edwin, Sun, Junwei, Jacobs, Jonathan, Dell’Osso, Lou, Hertle, Richard, Ma, Jian-xing, Redmond, T. Michael, Zhu, Xiaosong, Hauck, Bernd, Zelenaia, Olga, Shindler, Kenneth S., Maguire, Maureen G., Wright, J. Fraser, Volpe, Nicholas J., McDonnell, Jennifer Wellman, Auricchio, Alberto, High, Katherine A., Bennett, Jean
Publicado em 2008

Age-dependent effects of RPE65 gene therapy for Leber’s congenital amaurosis: a phase 1 dose-escalation trial

Por Maguire, Albert M, High, Katherine A, Auricchio, Alberto, Wright, J Fraser, Pierce, Eric A, Testa, Francesco, Mingozzi, Federico, Bennicelli, Jeannette L, Ying, Gui-shuang, Rossi, Settimio, Fulton, Ann, Marshall, Kathleen A, Banfi, Sandro, Chung, Daniel C, Morgan, Jessica IW, Hauck, Bernd, Zelenaia, Olga, Zhu, Xiaosong, Raffini, Leslie, Coppieters, Frauke, De Baere, Elfride, Shindler, Kenneth S, Volpe, Nicholas J, Surace, Enrico M, Acerra, Carmela, Lyubarsky, Arkady, Redmond, T Michael, Stone, Edwin, Sun, Junwei, McDonnell, Jennifer Wellman, Leroy, Bart P, Simonelli, Francesca, Bennett, Jean
Publicado no Lancet (2009)