The leak stops here: platelets as delivery vehicles for coagulation factors

द्वारा High, Katherine A.
प्रकाशित 2006

Theodore E. Woodward Award. AAV-mediated gene transfer for hemophilia.

द्वारा High, Katherine A.
प्रकाशित 2003

The Jeremiah Metzger Lecture: Gene Therapy for Inherited Disorders: From Christmas Disease to Leber's Amaurosis

द्वारा High, Katherine A.
प्रकाशित 2009

The gene therapy journey for hemophilia: are we there yet?

द्वारा High, Katherine A.
प्रकाशित 2012

Gene Therapy for Hemophilia: The Clot Thickens

द्वारा High, Katherine A.
में प्रकाशित Hum Gene Ther (2014)

Turning genes into medicines—what have we learned from gene therapy drug development in the past decade?

द्वारा High, Katherine A.
में प्रकाशित Nat Commun (2020)

Immune responses to AAV vectors: overcoming barriers to successful gene therapy

द्वारा Mingozzi, Federico, High, Katherine A.
प्रकाशित 2013

Gene therapy for haemophilia

द्वारा Murphy, Samuel L, High, Katherine A
प्रकाशित 2008

Cell Phones and Landlines: The Impact of Gene Therapy on the Cost and Availability of Treatment for Hemophilia

द्वारा High, Katherine A, Skinner, Mark W
प्रकाशित 2011

Adeno-associated viral vectors for the treatment of hemophilia

द्वारा High, Katherine A., Anguela, Xavier M.
में प्रकाशित Hum Mol Genet (2016)

Oracle or false prophet? Can we predict AAV efficacy based on preexisting antibody titers?

द्वारा Anguela, Xavier M., High, Katherine A.
में प्रकाशित Res Pract Thromb Haemost (2019)

A NlaIV polymorphism within the human Factor X gene

द्वारा Wallmark, Anders, Rose, Virgil L., Ho, Coty, High, Katherine A.
प्रकाशित 1991

A frequent human coagulation Factor VII mutation (A294V, c152) in loop 140s affects the interaction with activators, tissue factor and substrates.

द्वारा Toso, Raffaella, Pinotti, Mirko, High, Katherine A, Pollak, Eleanor S, Bernardi, Francesco
प्रकाशित 2002

Clinical development of gene therapy: results and lessons from recent successes

द्वारा Kumar, Sandeep RP, Markusic, David M, Biswas, Moanaro, High, Katherine A, Herzog, Roland W
में प्रकाशित Mol Ther Methods Clin Dev (2016)

Novel therapeutic approach for hemophilia using gene delivery of an engineered secreted activated Factor VII

द्वारा Margaritis, Paris, Arruda, Valder R., Aljamali, Majed, Camire, Rodney M., Schlachterman, Alexander, High, Katherine A.
प्रकाशित 2004

Gene Therapy Research at the Frontiers of Viral Immunology

द्वारा Hoffman, Brad E., Ertl, Hildegund C. J., Terhorst, Cox, High, Katherine A., Herzog, Roland W.
प्रकाशित 2012

Diverse IgG Subclass Responses to Adeno-associated Virus Infection and Vector Administration

द्वारा Murphy, Samuel L., Li, Hojun, Mingozzi, Federico, Sabatino, Denise, Hui, Danny, Edmonson, Shyrie, High, Katherine A.
प्रकाशित 2009

Successful Phenotype Improvement following Gene Therapy for Severe Hemophilia A in Privately Owned Dogs

द्वारा Callan, Mary Beth, Haskins, Mark E., Wang, Ping, Zhou, Shangzhen, High, Katherine A., Arruda, Valder R.
में प्रकाशित PLoS One (2016)

Enhanced Factor VIII Heavy Chain for Gene Therapy of Hemophilia A

द्वारा Chen, Lingxia, Lu, Hui, Wang, Jinhui, Sarkar, Rita, Yang, Xiao, Wang, Hongli, High, Katherine A, Xiao, Weidong
प्रकाशित 2009

Safety of Liver Gene Transfer Following Peripheral Intravascular Delivery of Adeno-Associated Virus (AAV)-5 and AAV-6 in a Large Animal Model

द्वारा Favaro, Patricia, Finn, Jonathan D., Siner, Joshua I., Wright, J. Fraser, High, Katherine A., Arruda, Valder R.
प्रकाशित 2011