Miglustat Treatment May Reduce Cerebrospinal Fluid Levels of the Axonal Degeneration Marker Tau in Niemann–Pick Type C

Introduction: Niemann–Pick disease type C (NPC) is a lysosomal storage disorder that leads to progressive neurodegeneration. The glucosylceramide synthase blocker miglustat is being used to treat NPC, but monitoring of disease progression and treatment response is difficult. NPC patients have elevat...

Descripción completa

Guardado en:
Detalles Bibliográficos
Autores principales: Mattsson, Niklas, Zetterberg, Henrik, Bianconi, Simona, Yanjanin, Nicole M., Fu, Rao, Månsson, Jan-Eric, Porter, Forbes D., Blennow, Kaj
Formato: Artigo
Lenguaje:Inglês
Publicado: Springer Berlin Heidelberg 2011
Materias:
Article
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC3509856/
https://ncbi.nlm.nih.gov/pubmed/23430872
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2011_47
Etiquetas: Agregar Etiqueta
Sin Etiquetas, Sea el primero en etiquetar este registro!

Ejemplares similares