The Human Rhodopsin Kinase Promoter in an AAV5 Vector Confers Rod- and Cone-Specific Expression in the Primate Retina

Adeno-associated virus (AAV) has proven an effective gene delivery vehicle for the treatment of retinal disease. Ongoing clinical trials using a serotype 2 AAV vector to express RPE65 in the retinal pigment epithelium have proven safe and effective. While many proof-of-concept studies in animal mode...

Descripció completa

Guardat en:
Dades bibliogràfiques
Autors principals: Boye, Shannon E., Alexander, John J., Boye, Sanford L., Witherspoon, Clark D., Sandefer, Kristen J., Conlon, Thomas J., Erger, Kirsten, Sun, Jingfen, Ryals, Renee, Chiodo, Vince A., Clark, Mark E., Girkin, Christopher A., Hauswirth, William W., Gamlin, Paul D.
Format: Artigo
Idioma:Inglês
Publicat: Mary Ann Liebert, Inc. 2012
Matèries:
Research Articles
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3472519/
https://ncbi.nlm.nih.gov/pubmed/22845794
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2012.125
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!

Ítems similars