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Misdiagnosis of Niemann-Pick disease type C as Gaucher disease

Niemann-Pick disease type C (NPC) is a model for inborn errors of metabolism whose gene product mediates molecular trafficking rather than catabolizing macromolecules, as in classic lipidoses. We report the case of an infant who presented with hepatosplenomegaly without neurological abnormalities. D...

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Main Authors: Lo, Sarah M., McNamara, Joseph, Seashore, Margherita R., Mistry, Pramod K.
Formato: Artigo
Idioma:Inglês
Publicado: 2010
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC3053412/
https://ncbi.nlm.nih.gov/pubmed/20882348
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s10545-010-9214-3
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