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Fabry disease: six gene rearrangements and an exonic point mutation in the alpha-galactosidase gene.

Fabry disease, an X-linked recessive disorder of glycosphingolipid catabolism, results from the deficient activity of the lysosomal hydrolase, alpha-galactosidase. Southern hybridization analysis of the alpha-galactosidase gene in affected hemizygous males from 130 unrelated families with Fabry dise...

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Autors principals: Bernstein, H S, Bishop, D F, Astrin, K H, Kornreich, R, Eng, C M, Sakuraba, H, Desnick, R J
Format: Artigo
Idioma:Inglês
Publicat: 1989
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC303833/
https://ncbi.nlm.nih.gov/pubmed/2539398
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