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Characterization of Genome Integrity for Oversized Recombinant AAV Vector

Application of recombinant adeno-associated virus (rAAV) in gene therapy has been limited by its packaging capacity. Recent studies suggested that rAAV could achieve persistent transgene expression beyond 4.7-kb packaging limit. To clarify the mechanism leading to transgene expression from oversized...

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Autores principales: Dong, Biao, Nakai, Hiroyuki, Xiao, Weidong
Formato: Artigo
Lenguaje:Inglês
Publicado: Nature Publishing Group 2009
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC2803017/
https://ncbi.nlm.nih.gov/pubmed/19904236
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2009.258
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