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The RPGRIP1-deficient dog, a promising canine model for gene therapy

PURPOSE: To evaluate the RPGRIP1-deficient miniature longhaired dachshund (MLHD) dog as a potential candidate for gene therapy. METHODS: Six RPGRIP1-deficient MLHD dogs from our dog colony have been observed for two years using a variety of noninvasive procedures. These included bilateral full-field...

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Библиографические подробности
Главные авторы: Lhériteau, Elsa, Libeau, Lyse, Stieger, Knut, Deschamps, Jack-Yves, Mendes-Madeira, Alexandra, Provost, Nathalie, Lemoine, Francoise, Mellersh, Cathryn, Ellinwood, N. Matthew, Cherel, Yan, Moullier, Philippe, Rolling, Fabienne
Формат: Artigo
Язык:Inglês
Опубликовано: Molecular Vision 2009
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC2642837/
https://ncbi.nlm.nih.gov/pubmed/19223988
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