Wird geladen...

PTC124 is an orally bioavailable compound that promotes suppression of the human CFTR-G542X nonsense allele in a CF mouse model

Nonsense mutations inactivate gene function and are the underlying cause of a large percentage of the individual cases of many genetic disorders. PTC124 is an orally bioavailable compound that promotes readthrough of premature translation termination codons, suggesting that it may have the potential...

Ausführliche Beschreibung

Gespeichert in:
Bibliographische Detailangaben
Hauptverfasser: Du, Ming, Liu, Xiaoli, Welch, Ellen M., Hirawat, Samit, Peltz, Stuart W., Bedwell, David M.
Format: Artigo
Sprache:Inglês
Veröffentlicht: National Academy of Sciences 2008
Schlagworte:
Online Zugang:https://ncbi.nlm.nih.gov/pmc/articles/PMC2538881/
https://ncbi.nlm.nih.gov/pubmed/18272502
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.0711795105
Tags: Tag hinzufügen
Keine Tags, Fügen Sie den ersten Tag hinzu!