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Nonviral delivery of synthetic siRNAs in vivo

Sequence-specific gene silencing using small interfering RNA (siRNA) is a Nobel prize–winning technology that is now being evaluated in clinical trials as a potentially novel therapeutic strategy. This article provides an overview of the major pharmaceutical challenges facing siRNA therapeutics, foc...

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Библиографические подробности
Главные авторы: Akhtar, Saghir, Benter, Ibrahim F.
Формат: Artigo
Язык:Inglês
Опубликовано: American Society for Clinical Investigation 2007
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC2096447/
https://ncbi.nlm.nih.gov/pubmed/18060020
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI33494
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