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Enhancement of SMN2 Exon 7 Inclusion by Antisense Oligonucleotides Targeting the Exon

Several strategies have been pursued to increase the extent of exon 7 inclusion during splicing of SMN2 (survival of motor neuron 2) transcripts, for eventual therapeutic use in spinal muscular atrophy (SMA), a genetic neuromuscular disease. Antisense oligonucleotides (ASOs) that target an exon or i...

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Autores principales: Hua, Yimin, Vickers, Timothy A, Baker, Brenda F, Bennett, C. Frank, Krainer, Adrian R
Formato: Artigo
Lenguaje:Inglês
Publicado: Public Library of Science 2007
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC1820610/
https://ncbi.nlm.nih.gov/pubmed/17355180
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pbio.0050073
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