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SHOX haploinsufficiency and overdosage: impact of gonadal function status

Since its discovery in 1997, knowledge about the SHOX gene has rapidly increased. In this review, we summarise clinical features and diagnostic and therapeutic implications in SHOX haploinsufficiency and overdosage. SHOX haploinsufficiency usually results in mesomelic short stature and Turner skelet...

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Autors principals: Ogata, T., Matsuo, N., Nishimura, G.
Format: Artigo
Idioma:Inglês
Publicat: BMJ Group 2001
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC1734713/
https://ncbi.nlm.nih.gov/pubmed/11134233
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/jmg.38.1.1
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