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In vitro correction of cystic fibrosis epithelial cell lines by small fragment homologous replacement (SFHR) technique

BACKGROUND: SFHR (small fragment homologous replacement)-mediated targeting is a process that has been used to correct specific mutations in mammalian cells. This process involves both chemical and cellular factors that are not yet defined. To evaluate potential of this technique for gene therapy it...

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Pubblicato in:BMC Med Genet
Autori principali: Sangiuolo, Federica, Bruscia, Emanuela, Serafino, Annalucia, Nardone, Anna Maria, Bonifazi, Emanuela, Lais, Monica, Gruenert, Dieter C, Novelli, Giuseppe
Natura: Artigo
Lingua:Inglês
Pubblicazione: BMC 2002
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Accesso online:https://ncbi.nlm.nih.govhttps://pmc.ncbi.nlm.nih.gov/articles/PMC130050/
https://ncbi.nlm.nih.govhttps://pubmed.ncbi.nlm.nih.gov/12243649/
https://ncbi.nlm.nih.govhttps://doi.org/10.1186/1471-2350-3-8
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