FDA approves leniolisib (Joenja) as the first treatment for APDS: A breaththrough in the field of immunology
Activated PI3K delta Syndrome (APDS) is a rare genetic heterogeneous disorder initially identified in 2013. The primary cause of APDS is an immune imbalance leading to immune deficiency and dysregulation. Symptoms of APDS are diverse primarily including recurrent respiratory infections and increased...
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| Principais autores: | , |
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| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
Elsevier
2024-01-01
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| coleção: | Rare |
| Assuntos: | |
| Acesso em linha: | http://www.sciencedirect.com/science/article/pii/S2950008724000115 |
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