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FDA approves leniolisib (Joenja) as the first treatment for APDS: A breaththrough in the field of immunology

Activated PI3K delta Syndrome (APDS) is a rare genetic heterogeneous disorder initially identified in 2013. The primary cause of APDS is an immune imbalance leading to immune deficiency and dysregulation. Symptoms of APDS are diverse primarily including recurrent respiratory infections and increased...

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Bibliografiske detaljer
Principais autores: Muhammad Talha, Mohammad Haris Ali
Format: Artigo
Sprog:Inglês
Udgivet: Elsevier 2024-01-01
Serier:Rare
Fag:
Online adgang:http://www.sciencedirect.com/science/article/pii/S2950008724000115
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