Thermal Stability as a Determinant of AAV Serotype Identity
Currently, there are over 150 ongoing clinical trials utilizing adeno-associated viruses (AAVs) to target various genetic diseases, including hemophilia (AAV2 and AAV8), congenital heart failure (AAV1 and AAV6), cystic fibrosis (AAV2), rheumatoid arthritis (AAV2), and Batten disease (AAVrh.10). Prio...
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| Autors principals: | , , , , , , , , |
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| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Elsevier
2017-09-01
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| Col·lecció: | Molecular Therapy: Methods & Clinical Development |
| Matèries: | |
| Accés en línia: | http://www.sciencedirect.com/science/article/pii/S2329050117300864 |
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