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Clinical Efficacy and Safety of Ivacaftor/Lumacaftor Combination in Patients with Cystic Fibrosis: International Studies Review

Cystic fibrosis is an autosomal recessive disease caused by structure abnormalities in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. It is characterized by severe course and poor prognosis without or with insufficient treatment. Approval of pathogenetic therapy medications, CF...

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Principais autores: Nataliya Yu. Kashirskaya, Nika V. Petrova, Rena A. Zinchenko
Formato: Artigo
Idioma:Inglês
Publicado em: "Paediatrician" Publishers LLC 2021-12-01
coleção:Вопросы современной педиатрии
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Acesso em linha:https://vsp.spr-journal.ru/jour/article/view/2794
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