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Clinical Efficacy and Safety of Ivacaftor/Lumacaftor Combination in Patients with Cystic Fibrosis: International Studies Review

Cystic fibrosis is an autosomal recessive disease caused by structure abnormalities in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. It is characterized by severe course and poor prognosis without or with insufficient treatment. Approval of pathogenetic therapy medications, CF...

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Detaylı Bibliyografya
Asıl Yazarlar: Nataliya Yu. Kashirskaya, Nika V. Petrova, Rena A. Zinchenko
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: "Paediatrician" Publishers LLC 2021-12-01
Seri Bilgileri:Вопросы современной педиатрии
Konular:
Online Erişim:https://vsp.spr-journal.ru/jour/article/view/2794
Etiketler: Etiketle
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