Update on Gene Therapy Clinical Trials for Choroideremia and Potential Experimental Therapies
<i>Background and objectives</i>: Choroideremia (CHM) is an X-linked recessive chorioretinal dystrophy caused by mutations involving the <i>CHM</i> gene. Gene therapy has entered late-phase clinical trials, although there have been variable results. This review gives a summary on the outcomes of pha...
Wedi'i Gadw mewn:
| Prif Awduron: | , , , |
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| Fformat: | Artigo |
| Iaith: | Inglês |
| Cyhoeddwyd: |
MDPI AG
2021-01-01
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| Cyfres: | Medicina |
| Pynciau: | |
| Mynediad Ar-lein: | https://www.mdpi.com/1648-9144/57/1/64 |
| Tagiau: |
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