Update on Gene Therapy Clinical Trials for Choroideremia and Potential Experimental Therapies
<i>Background and objectives</i>: Choroideremia (CHM) is an X-linked recessive chorioretinal dystrophy caused by mutations involving the <i>CHM</i> gene. Gene therapy has entered late-phase clinical trials, although there have been variable results. This review gives a summary on the outcomes of pha...
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| Principais autores: | , , , |
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| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
MDPI AG
2021-01-01
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| coleção: | Medicina |
| Assuntos: | |
| Acesso em linha: | https://www.mdpi.com/1648-9144/57/1/64 |
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