Simian immundeficiency virus lentivector corrects human X-linked chronic granulomatous disease in the NOD/SCID mouse xenograft

Por Naumann, Nora, De Ravin, Suk See, Choi, Uimook, Moayeri, Morvarid, Whiting-Theobald, Narda, Linton, Gilda F., Ikeda, Yasuhiro, Malech, Harry L.
Publicado em 2007

WHIM syndrome myelokathexis reproduced in the NOD/SCID mouse xenotransplant model engrafted with healthy human stem cells transduced with C-terminus–truncated CXCR4

Por Kawai, Toshinao, Choi, Uimook, Cardwell, Lanise, DeRavin, Suk See, Naumann, Nora, Whiting-Theobald, Narda L., Linton, Gilda F., Moon, Jaehyun, Murphy, Philip M., Malech, Harry L.
Publicado em 2007

Correction of canine X-linked severe combined immunodeficiency by in vivo retroviral gene therapy

Por Ravin, Suk See Ting–De, Kennedy, Douglas R., Naumann, Nora, Kennedy, Jeffrey S., Choi, Uimook, Hartnett, Brian J., Linton, Gilda F., Whiting-Theobald, Narda L., Moore, Peter F., Vernau, William, Malech, Harry L., Felsburg, Peter J.
Publicado em 2006

Gene therapy improves immune function in preadolescents with X-linked severe combined immunodeficiency

Por Chinen, Javier, Davis, Joie, De Ravin, Suk See, Hay, Beverly N., Hsu, Amy P., Linton, Gilda F., Naumann, Nora, Nomicos, Effie Y. H., Silvin, Christopher, Ulrick, Jean, Whiting-Theobald, Narda L., Malech, Harry L., Puck, Jennifer M.
Publicado em 2007

Hypomorphic Rag mutations can cause destructive midline granulomatous disease

Por De Ravin, Suk See, Cowen, Edward W., Zarember, Kol A., Whiting-Theobald, Narda L., Kuhns, Douglas B., Sandler, Netanya G., Douek, Daniel C., Pittaluga, Stefania, Poliani, Pietro L., Lee, Yu Nee, Notarangelo, Luigi D., Wang, Lei, Alt, Frederick W., Kang, Elizabeth M., Milner, Joshua D., Niemela, Julie E., Fontana-Penn, Mary, Sinal, Sara H., Malech, Harry L.
Publicado em 2010

Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease

Por Malech, Harry L., Maples, Phillip B., Whiting-Theobald, Narda, Linton, Gilda F., Sekhsaria, Sudhir, Vowells, Sarah J., Li, Fei, Miller, Judi A., DeCarlo, Ellen, Holland, Steven M., Leitman, Susan F., Carter, Charles S., Butz, Robert E., Read, Elizabeth J., Fleisher, Thomas A., Schneiderman, Richard D., Van Epps, Dennis E., Spratt, S. Kaye, Maack, Christopher A., Rokovich, Joseph A., Cohen, Lawrence K., Gallin, John I.
Publicado em 1997