Careful adjustment of Epo non-viral gene therapy for β-thalassemic anaemia treatment

Por Fabre, Emmanuelle E, Bigey, Pascal, Beuzard, Yves, Scherman, Daniel, Payen, Emmanuel
Publicado em 2008

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

Por Cavazzana-Calvo, Marina, Fischer, Alain, Bushman, Frederic D., Payen, Emmanuel, Hacein-Bey-Abina, Salima, Leboulch, Philippe
Publicado em 2011

High-Efficiency Transduction of Primary Human Hematopoietic Stem/Progenitor Cells by AAV6 Vectors: Strategies for Overcoming Donor-Variation and Implications in Genome Editing

Por Ling, Chen, Bhukhai, Kanit, Yin, Zifei, Tan, Mengqun, Yoder, Mervin C., Leboulch, Philippe, Payen, Emmanuel, Srivastava, Arun
Publicado no Sci Rep (2016)

Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion

Por Negre, Olivier, Fusil, Floriane, Colomb, Charlotte, Roth, Shoshannah, Gillet-Legrand, Beatrix, Henri, Annie, Beuzard, Yves, Bushman, Frederic, Leboulch, Philippe, Payen, Emmanuel
Publicado em 2011

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene

Por Negre, Olivier, Eggimann, Anne-Virginie, Beuzard, Yves, Ribeil, Jean-Antoine, Bourget, Philippe, Borwornpinyo, Suparerk, Hongeng, Suradej, Hacein-Bey, Salima, Cavazzana, Marina, Leboulch, Philippe, Payen, Emmanuel
Publicado no Hum Gene Ther (2016)

Distribution of Lentiviral Vector Integration Sites in Mice Following Therapeutic Gene Transfer to Treat β-thalassemia

Por Ronen, Keshet, Negre, Olivier, Roth, Shannah, Colomb, Charlotte, Malani, Nirav, Denaro, Maria, Brady, Troy, Fusil, Floriane, Gillet-Legrand, Beatrix, Hehir, Kathleen, Beuzard, Yves, Leboulch, Philippe, Down, Julian D, Payen, Emmanuel, Bushman, Frederic D
Publicado em 2011

Permanent and panerythroid correction of murine β thalassemia by multiple lentiviral integration in hematopoietic stem cells

Por Imren, Suzan, Payen, Emmanuel, Westerman, Karen A., Pawliuk, Robert, Fabry, Mary E., Eaves, Connie J., Cavilla, Benjamin, Wadsworth, Louis D., Beuzard, Yves, Bouhassira, Eric E., Russell, Robert, London, Irving M., Nagel, Ronald L., Leboulch, Philippe, Humphries, R. Keith
Publicado em 2002

Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles

Por Prel, Anne, Caval, Vincent, Gayon, Régis, Ravassard, Philippe, Duthoit, Christine, Payen, Emmanuel, Maouche-Chretien, Leila, Creneguy, Alison, Nguyen, Tuan Huy, Martin, Nicolas, Piver, Eric, Sevrain, Raphaël, Lamouroux, Lucille, Leboulch, Philippe, Deschaseaux, Frédéric, Bouillé, Pascale, Sensébé, Luc, Pagès, Jean-Christophe
Publicado no Mol Ther Methods Clin Dev (2015)

Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice

Por Abed, Soumeya, Tubsuwan, Alisa, Chaichompoo, Porntip, Park, In Hyun, Pailleret, Alice, Benyoucef, Aïssa, Tosca, Lucie, De Dreuzy, Edouard, Paulard, Anais, Granger-Locatelli, Marine, Relouzat, Francis, Prost, Stéphane, Tachdjian, Gerard, Fucharoen, Suthat, Daley, George Q., Payen, Emmanuel, Chrétien, Stany, Leboulch, Philippe, Maouche-Chrétien, Leïla
Publicado no Haematologica (2015)

Preclinical Evaluation of Efficacy and Safety of an Improved Lentiviral Vector for the Treatment of β-Thalassemia and Sickle Cell Disease

Por Negre, Olivier, Bartholomae, Cynthia, Beuzard, Yves, Cavazzana, Marina, Christiansen, Lauryn, Courne, Céline, Deichmann, Annette, Denaro, Maria, de Dreuzy, Edouard, Finer, Mitchell, Fronza, Raffaele, Gillet-Legrand, Béatrix, Joubert, Christophe, Kutner, Robert, Leboulch, Philippe, Maouche, Leïla, Paulard, Anaïs, Pierciey, Francis J., Rothe, Michael, Ryu, Byoung, Schmidt, Manfred, von Kalle, Christof, Payen, Emmanuel, Veres, Gabor
Publicado no Curr Gene Ther (2015)

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Por Cavazzana-Calvo, Marina, Payen, Emmanuel, Negre, Olivier, Wang, Gary, Hehir, Kathleen, Fusil, Floriane, Down, Julian, Denaro, Maria, Brady, Troy, Westerman, Karen, Cavallesco, Resy, Gillet-Legrand, Beatrix, Caccavelli, Laure, Sgarra, Riccardo, Maouche-Chrétien, Leila, Bernaudin, Françoise, Girot, Robert, Dorazio, Ronald, Mulder, Geert-Jan, Polack, Axel, Bank, Arthur, Soulier, Jean, Larghero, Jérôme, Kabbara, Nabil, Dalle, Bruno, Gourmel, Bernard, Socie, Gérard, Chrétien, Stany, Cartier, Nathalie, Aubourg, Patrick, Fischer, Alain, Cornetta, Kenneth, Galacteros, Frédéric, Beuzard, Yves, Gluckman, Eliane, Bushman, Frederick, Hacein-Bey-Abina, Salima, Leboulch, Philippe
Publicado em 2010